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A retrospective survey of patients with hereditary transthyretin-mediated (hATTR) amyloidosis treated with patisiran in real-world clinical practice in Belgium.

Authors :
De Bleecker, Jan L
Claeys, Kristl G
Delstanche, Stéphanie
Van Parys, Vinciane
Baets, Jonathan
Tilleux, Sebastien
Remiche, Gauthier
De Bleecker, Jan L
Claeys, Kristl G
Delstanche, Stéphanie
Van Parys, Vinciane
Baets, Jonathan
Tilleux, Sebastien
Remiche, Gauthier
Source :
Acta neurologica belgica, 123 (3
Publication Year :
2023

Abstract

Hereditary transthyretin-mediated (hATTR) amyloidosis, a genetic disease caused by mutations in the transthyretin gene, leads to progressive sensory and autonomic neuropathy and/or cardiomyopathy and is associated with renal and ophthalmologic manifestations and a poor prognosis.<br />SCOPUS: ar.j<br />info:eu-repo/semantics/published

Details

Database :
OAIster
Journal :
Acta neurologica belgica, 123 (3
Notes :
1 full-text file(s): application/pdf, English
Publication Type :
Electronic Resource
Accession number :
edsoai.on1411672199
Document Type :
Electronic Resource