Fast forward for gene therapy

Gene therapy has focused in the past on ex vivo studies for rare diseases, but approval of three proposals for in vivo studies of cystic fibrosis by the Recombinant DNA Advisory Committee of the National Institutes of Health may change this. Gene therapy is having mixed results in at least 15 trials nationwide. European researchers may gain ground on American researchers in 1993. Dutch and Italian investigators are attempting to target stem cells to prolong treatment for genetic disease resulting in adenine deaminase deficiency.