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P1543: MITAPIVAT DECREASES THE NEED FOR TRANSFUSIONS SECONDARY TO POORLY TOLERATED ANEMIA AND ACUTE EVENTS COMPARED TO PLACEBO IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED
- Source :
- HemaSphere, Vol 6, Pp 1424-1425 (2022)
- Publication Year :
- 2022
- Publisher :
- Wiley, 2022.
- Subjects :
- Diseases of the blood and blood-forming organs
RC633-647.5
Subjects
Details
- Language :
- English
- ISSN :
- 25729241
- Volume :
- 6
- Database :
- Directory of Open Access Journals
- Journal :
- HemaSphere
- Publication Type :
- Academic Journal
- Accession number :
- edsdoj.6304786c0b8244359be21dc929445656
- Document Type :
- article
- Full Text :
- https://doi.org/10.1097/01.HS9.0000849028.24492.c6