P021: Long-term follow-up of cipaglucosidase alfa/miglustat in ambulatory and non-ambulatory patients with Pompe disease: An open-label phase I/II study (ATB200-02)

Subjects

Subjects :

Genetics
QH426-470
Medicine

Details

Language :

English

ISSN :

29497744

Volume :

1

Issue :

1

Database :

Directory of Open Access Journals

Journal :

Genetics in Medicine Open

Publication Type :

Academic Journal

Accession number :

edsdoj.41cbbd3dd64e477caa62c2aca904b5de

Document Type :

article

Full Text :

https://doi.org/10.1016/j.gimo.2023.100031