P012: Pegtibatinase, an investigational enzyme replacement therapy for the treatment of classical homocystinuria: Latest findings from the COMPOSE phase 1/2 trial

Subjects

Subjects :

Genetics
QH426-470
Medicine

Details

Language :

English

ISSN :

29497744

Volume :

2

Issue :

100889-

Database :

Directory of Open Access Journals

Journal :

Genetics in Medicine Open

Publication Type :

Academic Journal

Accession number :

edsdoj.3c3e02c8f0154487a18dfd9490fcced4

Document Type :

article

Full Text :

https://doi.org/10.1016/j.gimo.2024.100889