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Direct intra-brain lentiviral-mediated gene delivery leads to widespread transgene distribution and high-level enzymatic correction in the whole CNS of Twitcher mouse
Authors :
Lattanzi, A.
Maderna, C.
Amendola, M.
Sergi Sergi, L.
Conti, D.
Orlacchio, Aldo
Martino, Sabata
Naldini, L.
Gritti, A.
Publication Year :
2009
Subjects
Subjects :
krabbe disease
Details
Language :
English
Database :
OpenAIRE
Accession number :
edsair.od......3982..e0bc5fa144b4eb9a847cdfe9cc34b071
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