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Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice
- Authors :
- Wein, N
Vulin, A
Falzarano, Ms
Szigyarto, Ca
Maiti, B
Findlay, A
Heller, Kn
Uhlén, M
Bakthavachalu, B
Messina, Sonia
Vita, Giuseppe
Passarelli, C
Gualandi, F
Wilton, Sd
Rodino Klapac LR
Yang, L
Dunn, Dm
Schoenberg, Dr
Weiss, Rb
Howard, Mt
Ferlini, A
Flanigan, K. M.
- Publication Year :
- 2014
Details
- Language :
- English
- Database :
- OpenAIRE
- Accession number :
- edsair.od......3978..ec97182f2b9721b1706a6cfd8d09c5b5