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Outcomes in children with hemophilia A with inhibitors: Results from a noninterventional study

Authors :
Michaela Lehle
Elena Santagostino
Maria Elisa Mancuso
Sammy Chebon
Johnny Mahlangu
Rebecca Kruse-Jarres
Nives Selak Bienz
Sylvia von Mackensen
Víctor Jiménez-Yuste
Johannes Oldenburg
Peter Trask
Gallia G. Levy
Elina Asikanius
Midori Shima
UAM. Departamento de Medicina
Instituto de Investigación Sanitaria Hospital Universitario de La Paz (IdiPAZ)
Source :
Biblos-e Archivo. Repositorio Institucional de la UAM, instname, Biblos-e Archivo: Repositorio Institucional de la UAM, Universidad Autónoma de Madrid
Publication Year :
2019

Abstract

Background: Data regarding management of pediatric persons with hemophilia A (PwHA) with factor VIII (FVIII) inhibitors are limited. This prospective noninterventional study (NCT02476942) evaluated annualized bleeding rates (ABRs), safety, and health-related quality of life (HRQoL) in pediatric PwHA with FVIII inhibitors. Procedure: PwHA aged<br />Was funded by F. Hoffmann-La Roche Ltd.

Details

ISSN :
15455017
Volume :
67
Issue :
10
Database :
OpenAIRE
Journal :
Pediatric bloodcancerREFERENCES
Accession number :
edsair.doi.dedup.....b4530e3089954b7a6d0ecfb3e3aaf2fd