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Targeting DNA Damage Response and Replication Stress in Pancreatic Cancer

Authors :
Stephan B. Dreyer
Rosie Upstill-Goddard
Viola Paulus-Hock
Clara Paris
Eirini-Maria Lampraki
Eloise Dray
Bryan Serrels
Giuseppina Caligiuri
Selma Rebus
Dennis Plenker
Zachary Galluzzo
Holly Brunton
Richard Cunningham
Mathias Tesson
Craig Nourse
Ulla-Maja Bailey
Marc Jones
Kim Moran-Jones
Derek W. Wright
Fraser Duthie
Karin Oien
Lisa Evers
Colin J. McKay
Grant A. McGregor
Aditi Gulati
Rachel Brough
Ilirjana Bajrami
Stephan Pettitt
Michele L. Dziubinski
Juliana Candido
Frances Balkwill
Simon T. Barry
Robert Grützmann
Lola Rahib
Amber Johns
Marina Pajic
Fieke E.M. Froeling
Phillip Beer
Elizabeth A. Musgrove
Gloria M. Petersen
Alan Ashworth
Margaret C. Frame
Howard C. Crawford
Diane M. Simeone
Chris Lord
Debabrata Mukhopadhyay
Christian Pilarsky
David A. Tuveson
Susanna L. Cooke
Nigel B. Jamieson
Jennifer P. Morton
Owen J. Sansom
Peter J. Bailey
Andrew V. Biankin
David K. Chang
Sarah Allison
Dario Beraldi
Euan Cameron
Stephan Dreyer
Paul Grimwood
Shane Kelly
John Marshall
Sancha Martin
Brian McDade
Daniel McElroy
Donna Ramsay
Derek Wright
Marc D. Jones
Jane Hair
Paul Westwood
Nicola Williams
Amber L. Johns
Amanda Mawson
Christopher J. Scarlett
Mary-Anne L. Brancato
Sarah J. Rowe
Skye H. Simpson
Mona Martyn-Smith
Michelle T. Thomas
Lorraine A. Chantrill
Venessa T. Chin
Angela Chou
Mark J. Cowley
Jeremy L. Humphris
R. Scott Mead
Adnan M. Nagrial
Jessica Pettit
Mark Pinese
Ilse Rooman
Jianmin Wu
Jiang Tao
Renee DiPietro
Clare Watson
Angela Steinmann
Hong Ching Lee
Rachel Wong
Andreia V. Pinho
Marc Giry-Laterriere
Roger J. Daly
Robert L. Sutherland
Sean M. Grimmond
Nicola Waddell
Karin S. Kassahn
David K. Miller
Peter J. Wilson
Ann-Marie Patch
Sarah Song
Ivon Harliwong
Senel Idrisoglu
Ehsan Nourbakhsh
Suzanne Manning
Shivangi Wani
Milena Gongora
Matthew Anderson
Oliver Holmes
Conrad Leonard
Darrin Taylor
Scott Wood
Christina Xu
Katia Nones
J. Lynn Fink
Angelika Christ
Tim Bruxner
Nicole Cloonan
Felicity Newell
John V. Pearson
Peter Bailey
Michael Quinn
Shivashankar Nagaraj
Stephen Kazakoff
Nick Waddell
Keerthana Krisnan
Kelly Quek
David Wood
Jaswinder S. Samra
Anthony J. Gill
Nick Pavlakis
Alex Guminski
Christopher Toon
Ray Asghari
Neil D. Merrett
Darren Pavey
Amitabha Das
Peter H. Cosman
Kasim Ismail
Chelsie O’Connnor
Vincent W. Lam
Duncan McLeod
Henry C. Pleass
Arthur Richardson
Virginia James
James G. Kench
Caroline L. Cooper
David Joseph
Charbel Sandroussi
Michael Crawford
James Gallagher
Michael Texler
Cindy Forest
Andrew Laycock
Krishna P. Epari
Mo Ballal
David R. Fletcher
Sanjay Mukhedkar
Nigel A. Spry
Bastiaan DeBoer
Ming Chai
Nikolajs Zeps
Maria Beilin
Kynan Feeney
Nan Q. Nguyen
Andrew R. Ruszkiewicz
Chris Worthley
Chuan P. Tan
Tamara Debrencini
John Chen
Mark E. Brooke-Smith
Virginia Papangelis
Henry Tang
Andrew P. Barbour
Andrew D. Clouston
Patrick Martin
Thomas J. O’Rourke
Amy Chiang
Jonathan W. Fawcett
Kellee Slater
Shinn Yeung
Michael Hatzifotis
Peter Hodgkinson
Christopher Christophi
Mehrdad Nikfarjam
Angela Mountain
Victorian Cancer Biobank
James R. Eshleman
Ralph H. Hruban
Anirban Maitra
Christine A. Iacobuzio-Donahue
Richard D. Schulick
Christopher L. Wolfgang
Richard A. Morgan
Mary Hodgin
Aldo Scarpa
Rita T. Lawlor
Stefania Beghelli
Vincenzo Corbo
Maria Scardoni
Claudio Bassi
Margaret A. Tempero
Janet S. Graham
Basic (bio-) Medical Sciences
Source :
Dreyer, S B, Upstill-goddard, R, Paulus-hock, V, Paris, C, Lampraki, E, Dray, E, Serrels, B, Caligiuri, G, Rebus, S, Plenker, D, Galluzzo, Z, Brunton, H, Cunningham, R, Tesson, M, Nourse, C, Bailey, U, Jones, M, Moran-jones, K, Wright, D W, Duthie, F, Oien, K, Evers, L, Mckay, C J, Mcgregor, G A, Gulati, A, Brough, R, Bajrami, I, Pettitt, S, Dziubinski, M L, Candido, J, Balkwill, F, Barry, S T, Grützmann, R, Rahib, L, Johns, A, Pajic, M, Froeling, F E M, Beer, P, Musgrove, E A, Petersen, G M, Ashworth, A, Frame, M C, Crawford, H C, Simeone, D M, Lord, C, Mukhopadhyay, D, Pilarsky, C, Tuveson, D A, Cooke, S L, Jamieson, N B, Morton, J P, Sansom, O J, Bailey, P J, Biankin, A V, Chang, D K, Allison, S, Bailey, P J, Bailey, U, Biankin, A V, Beraldi, D, Brunton, H, Caligiuri, G, Cameron, E, Chang, D K, Cooke, S L, Cunningham, R, Dreyer, S, Grimwood, P, Kelly, S, Lampraki, E, Marshall, J, Martin, S, Mcdade, B, Mcelroy, D, Musgrove, E A, Nourse, C, Paulus-hock, V, Ramsay, D, Upstill-goddard, R, Wright, D W, Jones, M D, Evers, L, Rebus, S, Rahib, L, Serrels, B, Hair, J, Jamieson, N B, Mckay, C J, Westwood, P, Williams, N, Duthie, F, Biankin, A V, Johns, A L, Mawson, A, Chang, D K, Scarlett, C J, Brancato, M L, Rowe, S J, Simpson, S H, Martyn-smith, M, Thomas, M T, Chantrill, L A, Chin, V T, Chou, A, Cowley, M J, Humphris, J L, Jones, M D, Mead, R S, Nagrial, A M, Pajic, M, Pettit, J, Pinese, M, Rooman, I, Wu, J, Tao, J, Dipietro, R, Watson, C, Steinmann, A, Lee, H C, Wong, R, Pinho, A V, Giry-laterriere, M, Daly, R J, Musgrove, E A, Sutherland, R L, Grimmond, S M, Waddell, N, Kassahn, K S, Miller, D K, Wilson, P J, Patch, A, Song, S, Harliwong, I, Idrisoglu, S, Nourse, C, Nourbakhsh, E, Manning, S, Wani, S, Gongora, M, Anderson, M, Holmes, O, Leonard, C, Taylor, D, Wood, S, Xu, C, Nones, K, Fink, J L, Christ, A, Bruxner, T, Cloonan, N, Newell, F, Pearson, J V, Bailey, P, Quinn, M, Nagaraj, S, Kazakoff, S, Waddell, N, Krisnan, K, Quek, K, Wood, D, Samra, J S, Gill, A J, Pavlakis, N, Guminski, A, Toon, C, Asghari, R, Merrett, N D, Pavey, D, Das, A, Cosman, P H, Ismail, K, O’connnor, C, Lam, V W, Mcleod, D, Pleass, H C, Richardson, A, James, V, Kench, J G, Cooper, C L, Joseph, D, Sandroussi, C, Crawford, M, Gallagher, J, Texler, M, Forest, C, Laycock, A, Epari, K P, Ballal, M, Fletcher, D R, Mukhedkar, S, Spry, N A, Deboer, B, Chai, M, Zeps, N, Beilin, M, Feeney, K, Nguyen, N Q, Ruszkiewicz, A R, Worthley, C, Tan, C P, Debrencini, T, Chen, J, Brooke-smith, M E, Papangelis, V, Tang, H, Barbour, A P, Clouston, A D, Martin, P, O’rourke, T J, Chiang, A, Fawcett, J W, Slater, K, Yeung, S, Hatzifotis, M, Hodgkinson, P, Christophi, C, Nikfarjam, M, Mountain, A, Biobank, V C, Eshleman, J R, Hruban, R H, Maitra, A, Iacobuzio-donahue, C A, Schulick, R D, Wolfgang, C L, Morgan, R A, Hodgin, M, Scarpa, A, Lawlor, R T, Beghelli, S, Corbo, V, Scardoni, M, Bassi, C, Tempero, M A, Biankin, A V, Grimmond, S M, Chang, D K, Musgrove, E A, Jones, M D, Nourse, C, Jamieson, N B, Graham, J S, Biankin, A V, Chang, D K, Jamieson, N B & Graham, J S 2020, ' Targeting DNA Damage Response and Replication Stress in Pancreatic Cancer ', Gastroenterology, vol. 160, no. 1, pp. 362-377.e13 . https://doi.org/10.1053/j.gastro.2020.09.043, Gastroenterology
Publication Year :
2021

Abstract

Background & Aims Continuing recalcitrance to therapy cements pancreatic cancer (PC) as the most lethal malignancy, which is set to become the second leading cause of cancer death in our society. The study aim was to investigate the association between DNA damage response (DDR), replication stress, and novel therapeutic response in PC to develop a biomarker-driven therapeutic strategy targeting DDR and replication stress in PC. Methods We interrogated the transcriptome, genome, proteome, and functional characteristics of 61 novel PC patient–derived cell lines to define novel therapeutic strategies targeting DDR and replication stress. Validation was done in patient-derived xenografts and human PC organoids. Results Patient-derived cell lines faithfully recapitulate the epithelial component of pancreatic tumors, including previously described molecular subtypes. Biomarkers of DDR deficiency, including a novel signature of homologous recombination deficiency, cosegregates with response to platinum (P < .001) and PARP inhibitor therapy (P < .001) in vitro and in vivo. We generated a novel signature of replication stress that predicts response to ATR (P < .018) and WEE1 inhibitor (P < .029) treatment in both cell lines and human PC organoids. Replication stress was enriched in the squamous subtype of PC (P < .001) but was not associated with DDR deficiency. Conclusions Replication stress and DDR deficiency are independent of each other, creating opportunities for therapy in DDR-proficient PC and after platinum therapy.<br />Graphical abstract

Details

Language :
English
Database :
OpenAIRE
Journal :
Dreyer, S B, Upstill-goddard, R, Paulus-hock, V, Paris, C, Lampraki, E, Dray, E, Serrels, B, Caligiuri, G, Rebus, S, Plenker, D, Galluzzo, Z, Brunton, H, Cunningham, R, Tesson, M, Nourse, C, Bailey, U, Jones, M, Moran-jones, K, Wright, D W, Duthie, F, Oien, K, Evers, L, Mckay, C J, Mcgregor, G A, Gulati, A, Brough, R, Bajrami, I, Pettitt, S, Dziubinski, M L, Candido, J, Balkwill, F, Barry, S T, Grützmann, R, Rahib, L, Johns, A, Pajic, M, Froeling, F E M, Beer, P, Musgrove, E A, Petersen, G M, Ashworth, A, Frame, M C, Crawford, H C, Simeone, D M, Lord, C, Mukhopadhyay, D, Pilarsky, C, Tuveson, D A, Cooke, S L, Jamieson, N B, Morton, J P, Sansom, O J, Bailey, P J, Biankin, A V, Chang, D K, Allison, S, Bailey, P J, Bailey, U, Biankin, A V, Beraldi, D, Brunton, H, Caligiuri, G, Cameron, E, Chang, D K, Cooke, S L, Cunningham, R, Dreyer, S, Grimwood, P, Kelly, S, Lampraki, E, Marshall, J, Martin, S, Mcdade, B, Mcelroy, D, Musgrove, E A, Nourse, C, Paulus-hock, V, Ramsay, D, Upstill-goddard, R, Wright, D W, Jones, M D, Evers, L, Rebus, S, Rahib, L, Serrels, B, Hair, J, Jamieson, N B, Mckay, C J, Westwood, P, Williams, N, Duthie, F, Biankin, A V, Johns, A L, Mawson, A, Chang, D K, Scarlett, C J, Brancato, M L, Rowe, S J, Simpson, S H, Martyn-smith, M, Thomas, M T, Chantrill, L A, Chin, V T, Chou, A, Cowley, M J, Humphris, J L, Jones, M D, Mead, R S, Nagrial, A M, Pajic, M, Pettit, J, Pinese, M, Rooman, I, Wu, J, Tao, J, Dipietro, R, Watson, C, Steinmann, A, Lee, H C, Wong, R, Pinho, A V, Giry-laterriere, M, Daly, R J, Musgrove, E A, Sutherland, R L, Grimmond, S M, Waddell, N, Kassahn, K S, Miller, D K, Wilson, P J, Patch, A, Song, S, Harliwong, I, Idrisoglu, S, Nourse, C, Nourbakhsh, E, Manning, S, Wani, S, Gongora, M, Anderson, M, Holmes, O, Leonard, C, Taylor, D, Wood, S, Xu, C, Nones, K, Fink, J L, Christ, A, Bruxner, T, Cloonan, N, Newell, F, Pearson, J V, Bailey, P, Quinn, M, Nagaraj, S, Kazakoff, S, Waddell, N, Krisnan, K, Quek, K, Wood, D, Samra, J S, Gill, A J, Pavlakis, N, Guminski, A, Toon, C, Asghari, R, Merrett, N D, Pavey, D, Das, A, Cosman, P H, Ismail, K, O’connnor, C, Lam, V W, Mcleod, D, Pleass, H C, Richardson, A, James, V, Kench, J G, Cooper, C L, Joseph, D, Sandroussi, C, Crawford, M, Gallagher, J, Texler, M, Forest, C, Laycock, A, Epari, K P, Ballal, M, Fletcher, D R, Mukhedkar, S, Spry, N A, Deboer, B, Chai, M, Zeps, N, Beilin, M, Feeney, K, Nguyen, N Q, Ruszkiewicz, A R, Worthley, C, Tan, C P, Debrencini, T, Chen, J, Brooke-smith, M E, Papangelis, V, Tang, H, Barbour, A P, Clouston, A D, Martin, P, O’rourke, T J, Chiang, A, Fawcett, J W, Slater, K, Yeung, S, Hatzifotis, M, Hodgkinson, P, Christophi, C, Nikfarjam, M, Mountain, A, Biobank, V C, Eshleman, J R, Hruban, R H, Maitra, A, Iacobuzio-donahue, C A, Schulick, R D, Wolfgang, C L, Morgan, R A, Hodgin, M, Scarpa, A, Lawlor, R T, Beghelli, S, Corbo, V, Scardoni, M, Bassi, C, Tempero, M A, Biankin, A V, Grimmond, S M, Chang, D K, Musgrove, E A, Jones, M D, Nourse, C, Jamieson, N B, Graham, J S, Biankin, A V, Chang, D K, Jamieson, N B & Graham, J S 2020, ' Targeting DNA Damage Response and Replication Stress in Pancreatic Cancer ', Gastroenterology, vol. 160, no. 1, pp. 362-377.e13 . https://doi.org/10.1053/j.gastro.2020.09.043, Gastroenterology
Accession number :
edsair.doi.dedup.....73a3f9673fbfb1bdd5184962a42fdfee
Full Text :
https://doi.org/10.1053/j.gastro.2020.09.043