Four-year follow-up from the ENCORE trial: A randomized, controlled, non-inferiority study comparing eliglustat to imiglucerase in patients with Gaucher disease type 1 stabilized on enzyme replacement therapy

Subjects

Subjects :

Pediatrics
medicine.medical_specialty
Imiglucerase
business.industry
Endocrinology, Diabetes and Metabolism
Disease
Enzyme replacement therapy
Biochemistry
Surgery
Endocrinology
Non inferiority
Genetics
medicine
In patient
business
Molecular Biology
Eliglustat
medicine.drug

Details

ISSN :

10967192

Volume :

117

Database :

OpenAIRE

Journal :

Molecular Genetics and Metabolism

Accession number :

edsair.doi...........dbc7c89e58bb71072c53cea1b5c0862b

Full Text :

https://doi.org/10.1016/j.ymgme.2015.12.229