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Intrathecal and intranasal infusion of adeno-associated virus vector: non-invasive routes of administration achieving corrective levels of iduronidase expression throughout the brain for gene therapy of mucopolysaccharidosis type I
Intrathecal and intranasal infusion of adeno-associated virus vector: non-invasive routes of administration achieving corrective levels of iduronidase expression throughout the brain for gene therapy of mucopolysaccharidosis type I
- Source :
- Molecular Genetics and Metabolism. 111:S75-S76
- Publication Year :
- 2014
- Publisher :
- Elsevier BV, 2014.
- Subjects :
- business.industry
Endocrinology, Diabetes and Metabolism
Genetic enhancement
Non invasive
Pharmacology
medicine.disease_cause
Intrathecal
Biochemistry
Virology
Mucopolysaccharidosis type I
Endocrinology
Genetics
medicine
Nasal administration
Vector (molecular biology)
business
Iduronidase
Molecular Biology
Adeno-associated virus
Subjects
Details
- ISSN :
- 10967192
- Volume :
- 111
- Database :
- OpenAIRE
- Journal :
- Molecular Genetics and Metabolism
- Accession number :
- edsair.doi...........d14b2c535094e3888486e051e0122f17
- Full Text :
- https://doi.org/10.1016/j.ymgme.2013.12.174