Profile of patients with mucopolysaccharidosis type II without cognitive impairment who started idursulfase treatment aged &gt/;20 years: data on late treatment initiation from the Hunter Outcome Survey (HOS)

Subjects

Subjects :

Pediatrics
medicine.medical_specialty
business.industry
Idursulfase
Endocrinology, Diabetes and Metabolism
Biochemistry
Endocrinology
Genetics
Physical therapy
Medicine
Mucopolysaccharidosis type II
business
Cognitive impairment
Molecular Biology
medicine.drug

Details

ISSN :

10967192

Volume :

120

Database :

OpenAIRE

Journal :

Molecular Genetics and Metabolism

Accession number :

edsair.doi...........cb674c39c592734b1b14afcebe1b28f1

Full Text :

https://doi.org/10.1016/j.ymgme.2016.11.194