Long-term benefit of sebelipase alfa over 76 weeks in children and adults with lysosomal acid lipase deficiency (LALD) 'ARISE'

Authors :: Katryn N. Furuya
Radhika Tripuraneni
Barbara K. Burton
Mark Friedman
Sachin Marulkar
Source :: Molecular Genetics and Metabolism. 120:S33
Publication Year :: 2017
Publisher :: Elsevier BV, 2017.

Subjects :: medicine.medical_specialty
business.industry
Endocrinology, Diabetes and Metabolism
030204 cardiovascular system & hematology
Lysosomal acid lipase deficiency
medicine.disease
Biochemistry
03 medical and health sciences
0302 clinical medicine
Endocrinology
Sebelipase alfa
Internal medicine
Genetics
medicine
030211 gastroenterology & hepatology
business
Molecular Biology

Full Text Access

Tools