Lenti-D Hematopoietic Stem Cell Gene Therapy to Arrest Progression of Cerebral Adrenoleukodystrophy: Interim Results of an International Phase 2/3 Trial

Subjects

Subjects :

Transplantation
medicine.anatomical_structure
business.industry
Genetic enhancement
Interim
Cancer research
medicine
Hematopoietic stem cell
Adrenoleukodystrophy
Hematology
business
medicine.disease

Details

ISSN :

10838791

Volume :

24

Database :

OpenAIRE

Journal :

Biology of Blood and Marrow Transplantation

Accession number :

edsair.doi...........c0a638242378286b2b93dd94cebe4be2

Full Text :

https://doi.org/10.1016/j.bbmt.2017.12.642