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Mini-COMET study: Safety, immunogenicity, and preliminary efficacy for repeat avalglucosidase alfa dosing in patients with infantile-onset Pompe disease (IOPD) who were previously treated with alglucosidase alfa and demonstrated clinical decline
- Source :
- Molecular Genetics and Metabolism. 129:S92
- Publication Year :
- 2020
- Publisher :
- Elsevier BV, 2020.
- Subjects :
- medicine.medical_specialty
business.industry
Endocrinology, Diabetes and Metabolism
Immunogenicity
Comet
Disease
Biochemistry
Gastroenterology
Endocrinology
Internal medicine
Genetics
Medicine
In patient
Infantile onset
Dosing
business
Previously treated
Molecular Biology
Alglucosidase alfa
medicine.drug
Subjects
Details
- ISSN :
- 10967192
- Volume :
- 129
- Database :
- OpenAIRE
- Journal :
- Molecular Genetics and Metabolism
- Accession number :
- edsair.doi...........b98ad4fdbcadaf86fea80c3187ade6a5