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Compassionate use of OTL-200 for patients with metachromatic leukodystrophy

Authors :
Paul J. Orchard
Ashish Gupta
Jennifer Braun
Laura A. Adang
Nishitha R. Pillai
Troy Lund
Julie B. Eisengart
Source :
Molecular Genetics and Metabolism. 138:107254
Publication Year :
2023
Publisher :
Elsevier BV, 2023.

Details

ISSN :
10967192
Volume :
138
Database :
OpenAIRE
Journal :
Molecular Genetics and Metabolism
Accession number :
edsair.doi...........b56e0b79df155f1ddfedc84ef5639276
Full Text :
https://doi.org/10.1016/j.ymgme.2022.107254