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VP.61 An AAV-shRNA DUX4-based therapy to treat facioscapulohumeral muscular dystrophy (FSHD)
- Source :
- Neuromuscular Disorders. 32:S107
- Publication Year :
- 2022
- Publisher :
- Elsevier BV, 2022.
Details
- ISSN :
- 09608966
- Volume :
- 32
- Database :
- OpenAIRE
- Journal :
- Neuromuscular Disorders
- Accession number :
- edsair.doi...........a3dee2b345b796c7ba9de0e0b14ebb72
- Full Text :
- https://doi.org/10.1016/j.nmd.2022.07.267