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VP.61 An AAV-shRNA DUX4-based therapy to treat facioscapulohumeral muscular dystrophy (FSHD)

Authors :
V. Mariot
E. Sidlauskaite
L. Le Gall
E. Corbex
J. Dumonceaux
Source :
Neuromuscular Disorders. 32:S107
Publication Year :
2022
Publisher :
Elsevier BV, 2022.

Details

ISSN :
09608966
Volume :
32
Database :
OpenAIRE
Journal :
Neuromuscular Disorders
Accession number :
edsair.doi...........a3dee2b345b796c7ba9de0e0b14ebb72
Full Text :
https://doi.org/10.1016/j.nmd.2022.07.267