A different type of genetic therapy: correcting a defective gene using antisense oligonucleotide treatment in CEP290 p.Cys998X LCA

Authors :: Julie De Zaeytijd
Bart P. Leroy
Artur V. Cideciyan
Stephen R. Russell
Wil den Hollander
Aniz Girach
Allen C. Ho
Alexandra V. Garafolo
Caroline Van Cauwenbergh
Arlene V. Drack
Samuel G. Jacobson
Fredrich Asmus
Alina V. Dumitrescu
Wanda L. Pfeifer
Michael R. Schwartz
Source :: Journal of American Association for Pediatric Ophthalmology and Strabismus. 25:e5
Publication Year :: 2021
Publisher :: Elsevier BV, 2021.

Subjects :: Ophthalmology
business.industry
Pediatrics, Perinatology and Child Health
Antisense oligonucleotides
Medicine
business
Gene
Molecular biology
Genetic therapy

ISSN :: 10918531
Volume :: 25
Database :: OpenAIRE
Journal :: Journal of American Association for Pediatric Ophthalmology and Strabismus
Accession number :: edsair.doi...........991be101297fd7e8846cbe3bcfc4af1d

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