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AAV-ARSA-mediated gene replacement for the treatment of metachromatic leukodystrophy

Authors :
Shyam Ramachandran
Jeffery Ardinger
Jie Bu
Swathi Ayloo
Amy M. Richards
Erik WIschhof
Jennifer Sullivan
Shelley Nass
Lilu Guo
Mariana Goncalves
Yinyin Huang
Qi Tang
Roger Trullo
Robert G. Jackson
Dinesh S. Bangari
Catherine O'Riordan
Martin Goulet
Christian Mueller
Source :
Molecular Genetics and Metabolism. 138:107284
Publication Year :
2023
Publisher :
Elsevier BV, 2023.

Subjects

Subjects :
Endocrinology
Endocrinology, Diabetes and Metabolism
Genetics
Molecular Biology
Biochemistry

Details

ISSN :
10967192
Volume :
138
Database :
OpenAIRE
Journal :
Molecular Genetics and Metabolism
Accession number :
edsair.doi...........95e74d42930aff2a6d43a54301810aff
Full Text :
https://doi.org/10.1016/j.ymgme.2022.107284
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