Gene editing to treat GM1-gangliosidosis by heterotopic insertion of GLB1 in a murine model

Authors :: Michael J. Przybilla
Li Ou
Chester B. Whitley
Jeanine R. Jarnes-Utz
Source :: Molecular Genetics and Metabolism. 129:S131
Publication Year :: 2020
Publisher :: Elsevier BV, 2020.

Subjects :: Endocrinology
GLB1
Genome editing
Murine model
Endocrinology, Diabetes and Metabolism
GM1 Gangliosidosis
Genetics
Cancer research
Biology
Molecular Biology
Biochemistry

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