Long-Term Durable FVIII Expression with Improvements in Bleeding Rates Following AAV-Mediated FVIII Gene Transfer for Hemophilia A: Multiyear Follow-up on the Phase I/II Trial of SPK-8011

Authors :: Stacy E. Croteau
M. Elaine Eyster
Huyen Tran
Margaret V. Ragni
Benjamin J. Samelson-Jones
Lindsey George
Spencer Sullivan
John E.J. Rasko
Jill Moormeier
Pantep Angchaisuksiri
Jerome Teitel
Gili Kenet
Tung Wynn
Kristen Jaworski
Amy Macdougall
Savina Jaeger
Trupti Trivedi
Federico Mingozzi
Tiffany Chang
Gallia Levy
Source :: Blood. 140:1899-1901
Publication Year :: 2022
Publisher :: American Society of Hematology, 2022.

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