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P1548: LONG-TERM TREATMENT WITH ORAL MITAPIVAT IS ASSOCIATED WITH NORMALIZATION OF HEMOGLOBIN LEVELS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY

Authors :
W. Barcellini
R. F. Grace
H. Al-Samkari
A. Glenthøj
J. A. Rothman
M. Morado Arias
D. M. Layton
O. Andres
M. DiBacco
P. Hawkins
M. P. Judge
F. Tai
J. Morales-Arias
V. Beynon
E. J. van Beers
Source :
HemaSphere. 6:1429-1430
Publication Year :
2022
Publisher :
Ovid Technologies (Wolters Kluwer Health), 2022.

Subjects

Subjects :
Hematology

Details

ISSN :
25729241
Volume :
6
Database :
OpenAIRE
Journal :
HemaSphere
Accession number :
edsair.doi...........7a758c7faa4f78673c8b7ad4b650114e