Back to Search Start Over

A phase 2a study to investigate the effect of a single dose of migalastat HCl, a pharmacological chaperone, on agalsidase activity in subjects with Fabry disease

Authors :
Myrl Holida
Kathy Nicholls
François Eyskens
Suma P. Shankar
Daniel G. Bichet
Majed Dasouki
Mark Thomas
Pol Boudes
Franklin K. Johnson
David G. Warnock
Ozlem Goker-Alpan
Source :
Molecular Genetics and Metabolism. 108:S96
Publication Year :
2013
Publisher :
Elsevier BV, 2013.

Abstract

David Warnock, Daniel Bichet, Myrl Holida, Ozlem Goker-Alpan, Kathy Nicholls, Mark Thomas, Francois Eyskens, Suma Shankar, Majed Dasouki, Franklin Johnson, Pol Boudes, University of Alabama at Birmingham, Birmingham, AL, USA, Hopital du Sacre-Coeur, Montreal, QC, Canada, University of Iowa Children's Hospital, Iowa City, IA, USA, O&O Alpan, LLC, Springfield, VA, USA, Royal Melbourne Hospital, Parkville, Australia, Linear Clinical Research, Perth WA, Australia, Universitair Ziekenhuis Antwerpen, Edegem, Belgium, Emory University, Decatur, GA, USA, University of Kansas, Kansas City, KS, USA, Amicus Therapeutics, Cranbury, NJ, USA

Details

ISSN :
10967192
Volume :
108
Database :
OpenAIRE
Journal :
Molecular Genetics and Metabolism
Accession number :
edsair.doi...........6d2bd4584490e8e5ab99a7d0b0f6a014
Full Text :
https://doi.org/10.1016/j.ymgme.2012.11.262