A qualitative study of the experience of venglustat for patients with Gaucher disease type 3 (GD3) in LEAP: A phase II open-label, multicenter, multinational study

Authors :: Ruth Pulikotil-Jacob
James Turnbull
Alaa Hamed
Camille Rochmann
Robert Krupnick
Chad Gwaltney
Ali Hariri
Source :: Molecular Genetics and Metabolism. 132:S91
Publication Year :: 2021
Publisher :: Elsevier BV, 2021.

Subjects :: medicine.medical_specialty
Endocrinology
business.industry
Endocrinology, Diabetes and Metabolism
Internal medicine
Genetics
Medicine
Disease
Open label
business
Molecular Biology
Biochemistry
Qualitative research

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