FIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy (SMA) (P7-9.009)

Authors :: Basil Darras
Giovanni Baranello
Odile Boespflug-Tanguy
John Day
Nicholas Deconinck
Andrea Klein
Ricardo Masson
Maria Mazurkiewicz-Bełdzińska
Eugenio Mercuri
Kristy Rose
Dmitry Vlodavets
Hui Xiong
Edmar Zanoteli
Muna El-Khairi
Marianne Gerber
Ksenija Gorni
Heidemarie Kletzl
Laura Palfreeman
Angela Dodman
Laurent Servais
Source :: Tuesday, April 25.
Publication Year :: 2023
Publisher :: Lippincott Williams & Wilkins, 2023.

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