A review of the clinical progression in six late onset Pompe disease (LOPD) patients following alglucosidase alfa cessation

Authors :: Andrew J. Oldham
Karolina M. Stepien
Mark E. Roberts
Reena Sharma
Source :: Molecular Genetics and Metabolism. 138:107245
Publication Year :: 2023
Publisher :: Elsevier BV, 2023.

Subjects :: Endocrinology
Endocrinology, Diabetes and Metabolism
Genetics
Molecular Biology
Biochemistry

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