592: Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR/Cas9 gene editing

Authors :: Patrick T. Harrison
Amy Walker
A. Aldossary
Stephen L. Hart
David J. Sanz
R. Maeshima
M. Woodall
R. McAnulty
D. J. Pearce
I. Guerrini
M. O’Hara-Wright
Deborah L. Baines
Christopher O'Callaghan
Source :: Journal of Cystic Fibrosis. 20:S281-S282
Publication Year :: 2021
Publisher :: Elsevier BV, 2021.

Subjects :: Pulmonary and Respiratory Medicine
Genetics
Genome editing
business.industry
Pediatrics, Perinatology and Child Health
RNA splicing
Mutation (genetic algorithm)
CRISPR
Medicine
business
medicine.disease
Cystic fibrosis

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