OP016: Mini-COMET: Safety and efficacy of ≥97 weeks’ avalglucosidase alfa in infantile-onset Pompe disease participants previously treated with alglucosidase alfa

Authors :: David Kronn
James Davison
Anaïs Brassier
Alexander Broomfield
Si Houn Hahn
Satoko Kumada
François Labarthe
Hirotaka Ohki
S. Grace Prakalapakorn
Kristina An Haack
Xianzhang Meng
Susan Sparks
Swathi Tammireddy
Catherine Wilson
Atef Zaher
Tianyue Zhou
Yin-Hsiu Chien
Priya Kishnani
null On behalf of the Mini-COMET investigators
Source :: Genetics in Medicine. 24:S348-S349
Publication Year :: 2022
Publisher :: Elsevier BV, 2022.

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