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Clinical event status of patients with Fabry disease after long-term treatment with agalsidase beta and follow-up from The Fabry Registry

Authors :
Dominique P. Germain
Marta Cizmarik
Frank Weidemann
David G. Warnock
Gabor E. Linthorst
William R. Wilcox
Source :
Molecular Genetics and Metabolism. 108:S42
Publication Year :
2013
Publisher :
Elsevier BV, 2013.

Details

ISSN :
10967192
Volume :
108
Database :
OpenAIRE
Journal :
Molecular Genetics and Metabolism
Accession number :
edsair.doi...........2bb542ad9dc610f47a6afdf46739f3c5
Full Text :
https://doi.org/10.1016/j.ymgme.2012.11.092