Analysis of pooled data from clinical trials in treatment-naïve patients with late-onset Pompe disease (LOPD) to inform on the efficacy of avalglucosidase alfa

Authors :: Tahseen Mozaffar
Lionel Riou França
Jerome Msihid
Pragya Shukla
Irina Proskorovsky
Tianyue Zhou
Marie Fournier
Magali Periquet
Kristina An Haack
Laurence Pollissard
Volker Straub
Source :: Molecular Genetics and Metabolism. 135:S86
Publication Year :: 2022
Publisher :: Elsevier BV, 2022.

Subjects :: Endocrinology
Endocrinology, Diabetes and Metabolism
Genetics
Molecular Biology
Biochemistry

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