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P040 Compassionate use triple therapy CFTR modulation (Kaftrio®) in severe disease. Single-centre, real-world clinical outcomes, safety and tolerability
P040 Compassionate use triple therapy CFTR modulation (Kaftrio®) in severe disease. Single-centre, real-world clinical outcomes, safety and tolerability
- Source :
- Journal of Cystic Fibrosis. 20:S50-S51
- Publication Year :
- 2021
- Publisher :
- Elsevier BV, 2021.
-
Abstract
- Objective: Patients (F508del/F508del or F508del/MF) with severe CF (ppFEV1
- Subjects :
- Pulmonary and Respiratory Medicine
medicine.medical_specialty
medicine.drug_class
business.industry
Antibiotics
medicine.disease
Cystic fibrosis
Pulmonary embolism
Sepsis
Clinical trial
Tolerability
Internal medicine
Pediatrics, Perinatology and Child Health
Cohort
medicine
Liver function
business
Subjects
Details
- ISSN :
- 15691993
- Volume :
- 20
- Database :
- OpenAIRE
- Journal :
- Journal of Cystic Fibrosis
- Accession number :
- edsair.doi...........08b8a35386fbdf600c2871d111ed0648
- Full Text :
- https://doi.org/10.1016/s1569-1993(21)01067-5