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SUNFISH Part 2: Efficacy and Safety of Risdiplam (RG7916) in Patients with Type 2 or Non-Ambulant Type 3 Spinal Muscular Atrophy (SMA)
- Authors :
- Mercuri, Eugenio
Barisic, Nina
Boespflug-Tanguy, Odile
Deconinck, Nicolas
Kostera-Pruszczyk, Anna
Riccardo Masson
Mazzone, Elena
Nascimento, Andres
Saito, Kayoko
Vlodavets, Dmitry
Vuillerot, Carole
Fuerst-Recktenwald, Sabine
Fuhrer, Sibylle
Gerber, Marianne
Gorni, Ksenija
Kletzl, Heidemarie
Martin, Carmen
Yeung, Wai Yin
Day, John W.
- Source :
- Web of Science
Details
- Database :
- OpenAIRE
- Journal :
- Web of Science
- Accession number :
- edsair.dedup.wf.001..614065481125a9a231cdd0c94c80e46a