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Comparable outcomes after busulfan- or treosulfan-based conditioning for allo-HSCT in children with ALL: results of FORUM

Authors :
Kalwak, Krzysztof
Moser, Laura M.
Pötschger, Ulrike
Bader, Peter
Kleinschmidt, Katharina
Meisel, Roland
Dalle, Jean-Hugues
Yesilipek, Akif
Balduzzi, Adriana
Krivan, Gergely
Goussetis, Evgenios
Staciuk, Raquel
Sedlacek, Petr
Pichler, Herbert
Svec, Peter
Gabriel, Melissa
Güngör, Tayfun
Bilic, Ernest
Buechner, Jochen
Renard, Marleen
Vettenranta, Kim
Ifversen, Marianne
Diaz-de-Heredia, Cristina
Stein, Jerry
Toporski, Jacek
Bierings, Marc
Peters, Christina
Ansari, Marc
Locatelli, Franco
Source :
Blood Advances; 20250101, Issue: Preprints
Publication Year :
2025

Abstract

•Chemotherapy conditioning with BU- or TREO-based regimens yields comparable outcomes for allo-HSCT in children with ALL.•Either regimen can be effectively and safely used in patients >4 years when TBI is contraindicated or unavailable.

Details

Language :
English
ISSN :
24739529 and 24739537
Issue :
Preprints
Database :
Supplemental Index
Journal :
Blood Advances
Publication Type :
Periodical
Accession number :
ejs68143770
Full Text :
https://doi.org/10.1182/bloodadvances.2024014548