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Adenine base editor–mediated correction of the common and severe IVS1-110 (G>A) β-thalassemia mutation
- Source :
- Blood; March 2023, Vol. 141 Issue: 10 p1169-1179, 11p
- Publication Year :
- 2023
-
Abstract
- •Adenine base editors efficiently correct the IVS1-110 (G>A) β-thalassemia–causing mutation.•Base editing efficiently corrects the β-thalassemic phenotype in vitro and in vivo.
Details
- Language :
- English
- ISSN :
- 00064971 and 15280020
- Volume :
- 141
- Issue :
- 10
- Database :
- Supplemental Index
- Journal :
- Blood
- Publication Type :
- Periodical
- Accession number :
- ejs61423835
- Full Text :
- https://doi.org/10.1182/blood.2022016629