Promise and Potential Peril With Lumacaftor for the Trafficking Defective Type 2 Long-QT Syndrome-Causative Variants, p.G604S, p.N633S, and p.R685P, Using Patient-Specific Re-Engineered Cardiomyocytes

Authors :: O’Hare, Bailey J.
John Kim, C.S.
Hamrick, Samantha K.
Ye, Dan
Tester, David J.
Ackerman, Michael J.
Source :: Circulation: Cardiovascular Genetics; October 2020, Vol. 13 Issue: 5 p466-475, 10p
Publication Year :: 2020
Abstract: Supplemental Digital Content is available in the text.

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