Patent Issued for Therapeutic genome editing in Wiskott-Aldrich syndrome and X-linked thrombocytopenia (USPTO 11643671).

The system of claim 1, wherein the vector and the nuclease or the nucleic acid encoding the nuclease are configured for co-delivery to a cell. Keywords: Bioengineering; Biotechnology; Blood Platelet Disorders; CRISPR; Clinical Trials and Studies; Drugs and Therapies; Enzymes and Coenzymes; Gene Editing; Gene Therapy; Genetics; Genome Editing; Health and Medicine; Hematologic Diseases and Conditions; Hematology; Hematopoietic; Hemic and Lymphatic Diseases and Conditions; Hemorrhagic Disorders; Immune System Diseases and Conditions; Immunologic Deficiency Syndromes; Inherited Blood Coagulation Disorders; Leukocyte Disorders; Leukopenia; Lymphopenia; Nuclease; Post-Trial Research; Seattle Children's Hospital; Stem Cell Research; Syndromes; Therapeutics; Therapy; Thrombocytopenia; Wiskott-Aldrich Syndrome; X-Linked Genetic Diseases and Conditions EN Bioengineering Biotechnology Blood Platelet Disorders CRISPR Clinical Trials and Studies Drugs and Therapies Enzymes and Coenzymes Gene Editing Gene Therapy Genetics Genome Editing Health and Medicine Hematologic Diseases and Conditions Hematology Hematopoietic Hemic and Lymphatic Diseases and Conditions Hemorrhagic Disorders Immune System Diseases and Conditions Immunologic Deficiency Syndromes Inherited Blood Coagulation Disorders Leukocyte Disorders Leukopenia Lymphopenia Nuclease Post-Trial Research Seattle Children's Hospital Stem Cell Research Syndromes Therapeutics Therapy Thrombocytopenia Wiskott-Aldrich Syndrome X-Linked Genetic Diseases and Conditions 634 634 1 05/29/23 20230509 NES 230509 2023 JUN 1 (NewsRx) -- By a News Reporter-Staff News Editor at Gene Therapy Weekly -- A patent by the inventors Khan, Iram (Issaquah, WA, US), Rawlings, David J. (Seattle, WA, US), filed on April 19, 2018, was published online on May 9, 2023, according to news reporting originating from Alexandria, Virginia, by NewsRx correspondents. [Extracted from the article]