Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia (EARLY-FA); Evaluating New Clinical Outcome Assessments in Children With Friedreich Ataxia to Facilitate Clinical Trial Design.

A new clinical trial, NCT06560346, has been launched to study the natural history and outcomes of children and young adults with Friedreich ataxia. The trial aims to understand the disease features and progression in order to inform future clinical trials. The study will collect data from participants with genetically confirmed Friedreich ataxia, as well as control participants, and will assess biomarkers and outcome measures. The trial is not yet recruiting and is expected to be completed by September 2028. [Extracted from the article]