Maralixibat-treated patients with Alagille syndrome (ALGS) demonstrate improved event-free survival in a natural history comparison with patients from the GALA database: application of real-world evidence analytics.

Authors :: Hansen, B. E.
Vandriel, S. M.
Vig, P.
Garner, W.
Li, L.-T.
She, H.
Wang, J.-S.
Gilbert, M. A.
Jankowska, I.
Czubkowski, P.
Gliwicz-Miedzińska, D.
Gonzales, E. M.
Jacquemin, E.
Bouligand, J.
Spinner, N. B.
Loomes, K. M.
Piccoli, D. A.
D'Antiga, L.
Nicastro, E.
Sokal, É.
Source :: Journal of Pediatric Gastroenterology & Nutrition; 2022 Supplement, Vol. 74, p670-673, 4p
Publication Year :: 2022

Full Text Access

Tools