Gene replacement therapy for spinal muscular atrophy: safety and preliminary efficacy in a Brazilian cohort.

MLA

Mendonça, Rodrigo Holanda, et al. “Gene Replacement Therapy for Spinal Muscular Atrophy: Safety and Preliminary Efficacy in a Brazilian Cohort.” Gene Therapy, vol. 31, no. 7–8, July 2024, pp. 391–99. EBSCOhost, https://doi.org/10.1038/s41434-024-00456-y.

APA

Mendonça, R. H., Ortega, A. B., Matsui, C., Jr, van der Linden, V., Kerstenetzky, M., Grossklauss, L. F., Silveira-Lucas, E. L., Polido, G. J., & Zanoteli, E. (2024). Gene replacement therapy for spinal muscular atrophy: safety and preliminary efficacy in a Brazilian cohort. Gene Therapy, 31(7–8), 391–399. https://doi.org/10.1038/s41434-024-00456-y

Chicago

Mendonça, Rodrigo Holanda, Adriana Banzzatto Ortega, Ciro Matsui Jr, Vanessa van der Linden, Marcelo Kerstenetzky, Luis Fernando Grossklauss, Elizabeth L Silveira-Lucas, Graziela Jorge Polido, and Edmar Zanoteli. 2024. “Gene Replacement Therapy for Spinal Muscular Atrophy: Safety and Preliminary Efficacy in a Brazilian Cohort.” Gene Therapy 31 (7–8): 391–99. doi:10.1038/s41434-024-00456-y.