Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party.

Authors :: Lum SH
Minkov M
Jones SA
Hazelaar S
Sirait T
Potter JE
Stepensky P
Garban F
Pichler H
Stein J
Kaya Z
Schulz A
Mellgren K
Diaz de Heredia C
Pochon C
Riesco S
Diaz MA
Michel G
Lindemans C
Gruhn B
Albert MH
Lankester AC
Neven B
Wynn R
Source :: Bone marrow transplantation [Bone Marrow Transplant] 2023 May; Vol. 58 (5), pp. 594-596. Date of Electronic Publication: 2023 Feb 14.
Publication Year :: 2023

Subjects :: Child
Humans
Wolman Disease
Hematopoietic Stem Cell Transplantation
Wolman Disease therapy

Full Text Access

Tools