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Therapies for lysosomal storage diseases: Principles, practice, and prospects for refinements based on evolving science.

Authors :
Grabowski GA
Mistry PK
Source :
Molecular genetics and metabolism [Mol Genet Metab] 2022 Sep-Oct; Vol. 137 (1-2), pp. 81-91. Date of Electronic Publication: 2022 Jul 30.
Publication Year :
2022

Subjects

Subjects :
Humans
Lysosomal Storage Diseases genetics
Lysosomal Storage Diseases therapy
Fabry Disease therapy
Mucopolysaccharidoses therapy

Details

Language :
English
ISSN :
1096-7206
Volume :
137
Issue :
1-2
Database :
MEDLINE
Journal :
Molecular genetics and metabolism
Publication Type :
Academic Journal
Accession number :
35933791
Full Text :
https://doi.org/10.1016/j.ymgme.2022.07.014
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