Spinal muscular atrophy: A modifiable disease emerges.

Authors :: Fitzgerald DA
Abel F
Jones KJ
Farrar MA
Source :: Paediatric respiratory reviews [Paediatr Respir Rev] 2018 Sep; Vol. 28, pp. 1-2. Date of Electronic Publication: 2018 Jul 12.
Publication Year :: 2018

Subjects :: Drug Costs
Genetic Therapy
Humans
Muscular Atrophy, Spinal complications
Muscular Atrophy, Spinal physiopathology
Noninvasive Ventilation
Oligonucleotides economics
Prognosis
Respiratory Insufficiency etiology
Survival of Motor Neuron 2 Protein
Muscular Atrophy, Spinal therapy
Oligonucleotides therapeutic use
Respiratory Insufficiency therapy

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