Sebelipase alfa (Kanuma) for lysosomal acid lipase deficiency.

Source :: The Medical letter on drugs and therapeutics [Med Lett Drugs Ther] 2016 Sep 26; Vol. 58 (1504), pp. e126-7. Date of Electronic Publication: 2016 Sep 26.
Publication Year :: 2016

Subjects :: Clinical Trials as Topic methods
Enzyme Replacement Therapy methods
Gastrointestinal Diseases chemically induced
Humans
Sterol Esterase metabolism
Wolman Disease metabolism
Sterol Esterase therapeutic use
Wolman Disease drug therapy

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