Success in Sight for Gene Editing.

The article explores advancements in Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) and CRISPR-associated protein 9 (Cas9) technology, highlighting its potential for treating genetic diseases of the retina. It discusses the successful application of CRISPR-Cas9 in vivo to target and improve cone photoreceptor function in patients with CEP290-associated inherited retinal degeneration, underscoring its transformative impact on therapeutic approaches for genetic eye diseases.