Long-term effectiveness of agalsidase alfa enzyme replacement in Fabry disease: A Fabry Outcome Survey analysis.

Subjects

Subjects :

*THERAPEUTIC use of enzymes
*ANGIOKERATOMA corporis diffusum
*HEALTH outcome assessment
*SPHINGOLIPIDOSES
*CLINICAL trials

Details

Language :

English

ISSN :

10967192

Volume :

114

Issue :

2

Database :

Academic Search Index

Journal :

Molecular Genetics & Metabolism

Publication Type :

Academic Journal

Accession number :

102001647

Full Text :

https://doi.org/10.1016/j.ymgme.2014.12.025