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5 results on '"Nusinersen -- Health aspects"'

1. Gene-Based Therapy for Rare Pediatric Neuromuscular Disorders Puts Transition-of-Care Issues in the Spotlight

Author

Rao, Vamshi K.

Subjects
Eteplirsen -- Health aspects, HIV infections -- Care and treatment -- Health aspects, Heart diseases -- Care and treatment -- Health aspects, Pediatric diseases -- Care and treatment -- Health aspects, Nusinersen -- Health aspects, Virus diseases -- Care and treatment -- Health aspects, Pediatrics -- Health aspects, Cardiovascular diseases, Infection, Health, Health care industry
Abstract

Rare diseases are defined as conditions that affect fewer than 200,000 people at any given time. One in 10 people in the United States, 350 million people worldwide, are affected [...]

Published
2019

2. COVID-19 pandemic: The concerns of pediatric neurologists

Author

Saini, Arushi and Suthar, Renu

Subjects
Severe acute respiratory syndrome -- Health aspects, Neurophysiology -- Health aspects, Coronaviruses -- Health aspects, Epidemics -- China, Nusinersen -- Health aspects, Virus diseases -- Health aspects, COVID-19 -- Health aspects, Health
Abstract

Byline: Arushi. Saini, Renu. Suthar Dear editor, The tsunami of severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) pandemic has hit hard to the world with a massive impact on healthcare [...]

Published
2020

3. Researchers at University of Iowa Release New Data on Spinal Muscular Atrophy (Scoliosis and spinal muscular atrophy in the new world of medical therapy: providing lumbar access for intrathecal treatment in patients previously treated or ...)

Subjects
Spinal muscular atrophy -- Care and treatment -- Health aspects, Physical fitness -- Health aspects, Scoliosis -- Care and treatment -- Health aspects, Nusinersen -- Health aspects, Obesity, Orthopedic surgery, Muscular atrophy, Surgery, Editors, Health
Abstract

2019 APR 20 (NewsRx) -- By a News Reporter-Staff News Editor at Obesity, Fitness & Wellness Week -- Data detailed on Neuromuscular Diseases and Conditions - Spinal Muscular Atrophy have [...]

Published
2019

4. New oligonucleotide analogues for therapeutic applications

Subjects
Eteplirsen -- Health aspects, Nusinersen -- Health aspects, Mipomersen -- Health aspects, Messenger RNA, Patisiran, Toxicity, Clinical trials, RNA, Enzymes, Business, international
Abstract

Scope: Therapeutic oligonucleotides (Th-ONs) are rapidly becoming highly important agents for hard to treat diseases. They target mRNA thereby changing protein expression. With four Th-ONs now in the clinic; Eteplirsen, [...]

Published
2019

5. Time running out for boy, 3, who needs wonder drug or will lose ability to walk; Aadi Wilson, from Leicestershire suffers from rare condition SMA Type 2, and a 'wonder drug' is not available because of its high cost

Subjects
Nusinersen -- Health aspects, Infection, Pharmaceutical industry, General interest, News, opinion and commentary, Spinraza (Medication) -- Health aspects
Abstract

Byline: Dave Burke Every morning toddler Aadi Wilson has to have air blown into his lungs, because they do not fully inflate on their own. The three-year-old suffers from a [...]

Published
2019

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