1. Importance of SPP1 genotype as a covariate in clinical trials in Duchenne muscular dystrophy
- Author
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Bello, L, Piva, L, Barp, A, Taglia, Andrea, Picillo, E, Vasco, Gessica, Pane, Marika, Previtali, Sc, Torrente, Y, Gazzerro, E, Motta, Mario, Grieco, Giovanni, Napolitano, S, Magri, F, D'Amico, Adele, Astrea, G, Messina, S, Sframeli, M, Vita, Gl, Boffi, Pietro, Mongini, T, Ferlini, A, Gualandi, F, Soraru', G, Ermani, M, Vita, G, Battini, R, Bertini, Enrico Silvio, Comi, Gp, Berardinelli, A, Minetti, C, Bruno, Carmelina, Mercuri, Eugenio Maria, Politano, L, Angelini, Carlo, Hoffman, Ep, Pegoraro, E., Pane, Marika (ORCID:0000-0002-4851-6124), Mercuri, Eugenio Maria (ORCID:0000-0002-9851-5365), Bello, L, Piva, L, Barp, A, Taglia, Andrea, Picillo, E, Vasco, Gessica, Pane, Marika, Previtali, Sc, Torrente, Y, Gazzerro, E, Motta, Mario, Grieco, Giovanni, Napolitano, S, Magri, F, D'Amico, Adele, Astrea, G, Messina, S, Sframeli, M, Vita, Gl, Boffi, Pietro, Mongini, T, Ferlini, A, Gualandi, F, Soraru', G, Ermani, M, Vita, G, Battini, R, Bertini, Enrico Silvio, Comi, Gp, Berardinelli, A, Minetti, C, Bruno, Carmelina, Mercuri, Eugenio Maria, Politano, L, Angelini, Carlo, Hoffman, Ep, Pegoraro, E., Pane, Marika (ORCID:0000-0002-4851-6124), and Mercuri, Eugenio Maria (ORCID:0000-0002-9851-5365)
- Abstract
To test the effect of the single nucleotide polymorphism -66 T>G (rs28357094) in the osteopontin gene (SPP1) on functional measures over 12 months in Duchenne muscular dystrophy (DMD).
- Published
- 2012