Search

Your search keyword '"Zumberge, Nicholas"' showing total 2 results
Start Over Author "Zumberge, Nicholas" Topic genetic transformation
2 results on '"Zumberge, Nicholas"'

1. Systemic gene transfer of scAAV9.U1a.hSGSH for MPS IIIA: tolerability and preliminary evidence for a biochemical effect.

Author

Flanigan, Kevin M., Truxal, Kristen V., McBride, Kim L., McNally, Kelly A., Kunkler, Krista L., Zumberge, Nicholas A., Martin, Lisa, Aylward, Shawn C., Corridore, Marco, McKee, Christopher, Fu, Haiyan, and McCarty, Douglas M.

Subjects
*GLYCOSAMINOGLYCANS, *GENETIC transformation, *BIOACCUMULATION, *CELL death, *COGNITIVE ability
Published
2017
Full Text
View/download PDF

2. Design of a phase I/II gene transfer clinical trial of rAAV9.CMV.hNAGLU for mucopolysaccharidosis type IIIB.

Author

McBride, Kim L., Truxal, Kristen, McNally, Kelly, Kunkler, Krista, Sherrod-Canaan, Tamar, Aylward, Shawn, Miller, Tim, Zumberge, Nicholas, Martin, Lisa, Corridore, Marco, McKee, Christopher, McCarty, Douglas, Fu, Haiyan, and Flanigan, Kevin

Subjects
*GENETIC transformation, *CLINICAL trials, *SANFILIPPO syndrome, *MUCOPOLYSACCHARIDOSIS, *CHILDREN'S health, *DIAGNOSIS, *THERAPEUTICS
Published
2016
Full Text
View/download PDF

Catalog

Books, media, physical & digital resources
See catalog results