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Your search keyword '"Gil Gonen-Yaacovi"' showing total 3 results
Start Over "Gil Gonen-Yaacovi" Topic blood coagulation factor viii
3 results on '"Gil Gonen-Yaacovi"'

1. ASC Therapeutics Announces Podium and Poster Presentations of IND-Enabling Studies for ASC618, a Second-Generation Gene Therapy for Hemophilia A, at the 25th ASGCT Meeting, May 16-19, 2022 in Washington, D.C

Subjects
Gene expression, Genes, Gene therapy, Hemophilia, Liver, Blood coagulation factor VIII, Business, Business, international
Abstract

* Podium presentation highlights significant transduction and transgene expression in pharmacokinetic studies in mice, non-human primates and a humanized liver model * Poster presentation focuses on pharmacology, toxicology and safety [...]

Published
2022

2. ASC Therapeutics Receives Key Regulatory Designations in U.S. and Europe to Advance its Second-Generation Gene Therapy for Hemophilia A

Subjects
United States. Food and Drug Administration, Genes, Orphan drugs, Gene therapy, Hemophilia -- Care and treatment, Blood coagulation factor VIII, Business, Business, international
Abstract

* Recent U.S. FDA's Fast-Track Designation * Recent European Medicines Agency's Positive Opinion on Orphan Medical Product Designation * Previous FDA's IND Clearance and FDA's Orphan Drug Designation MILPITAS, Calif. [...]

Published
2022

3. ASC Therapeutics and Professor Steven W. Pipe Publish Expert Review on Novel Gene Therapies of Hemophilia A

Subjects
Genes, Gene therapy, Protein biosynthesis, Hemophilia, Liver, Blood coagulation factor VIII, Business, Business, international
Abstract

* Second-generation gene therapies can increase protein synthesis and secretion * Minimizing cellular stress can increase durability of liver-targeted gene therapies * A peer-reviewed, open-access, comprehensive seminal review MILPITAS, Calif. [...]

Published
2022

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