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2. 2024 Update: European Consensus Statement on Gene Therapy for Spinal Muscular Atrophy

3. TOP-417 Machine learning can improve prediction of hepatitis B surface antigen seroclearance: A large multicentre cohort study in the United Kingdom

4. WED-471 Retrospective analysis of longitudinal data for UK adults living with chronic HBV: characteristics of the population on dual therapy

6. Bulbar function in spinal muscular atrophy (SMA): State of art and new challenges. 21st July 2023, Rome, Italy

8. Changes in abilities over the initial 12 months of nusinersen treatment for type II SMA

10. Alteration of circadian sleep-wake rhythm and salivary melatonin secretion in idiopathic/isolated REM sleep behavior disorder: preliminary evidence

11. Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy

12. Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

20. A Hawkes model with CARMA(p,q) intensity

21. Safety, tolerability and pharmacokinetics of eteplirsen in young boys aged 6–48 months with Duchenne muscular dystrophy amenable to exon 51 skipping

23. Ligamentous laxity in children with achondroplasia: Prevalence, joint involvement, and implications for early intervention strategies

26. Psychological factors and barriers to donating and receiving milk from human milk banks: A review

27. Gain and loss of upper limb abilities in Duchenne muscular dystrophy patients: A 24-month study

30. Sunfish parts 1 and 2: 4-year efficacy and safety data of risdiplam in types 2 and 3 spinal muscular atrophy (SMA)

33. Carboplatin and paclitaxel plus avelumab compared with carboplatin and paclitaxel in advanced or recurrent endometrial cancer (MITO END-3): a multicentre, open-label, randomised, controlled, phase 2 trial

34. 254th ENMC international workshop. Formation of a European network to initiate a European data collection, along with development and sharing of treatment guidelines for adult SMA patients. Virtual meeting 28 – 30 January 2022

35. The emerging spectrum of neurodevelopmental comorbidities in early-onset Spinal Muscular Atrophy

37. P196 Age at loss of ambulation in patients with DMD from the STRIDE registry and the CINRG natural history study: a matched cohort analysis

38. P211 Intravenous and intrathecal onasemnogene abeparvovec gene therapy in symptomatic and presymptomatic spinal muscular atrophy (SMA): long-term follow-up study

39. P120 Refining MRI pattern in sarcoglycanopathies: upper body pattern and new approaches to assess disease progression

42. P41 EMBARK, a Phase 3 trial evaluating safety and efficacy of delandistrogene moxeparvovec in DMD: study design and baseline characteristics

43. P198 Updated demographics and safety data from patients with nonsense mutation Duchenne muscular dystrophy receiving ataluren in the STRIDE registry

47. P147 Six-year long-term safety and efficacy of Golodirsen in patients with DMD vs mutation-matched external controls

49. P35 Two-year clinical outcomes with fordadistrogene movaparvovec (FM) for Duchenne muscular dystrophy (DMD) and contextualization with external controls

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